Muscular Dystrophy Coordinating Committee Meeting - 03/18/2024 | Muscular Dystrophy Coordinating Committee

Monday, March 18, 2024

12:00 PM - 4:00 PM ET
Virtual Only
Webcast Live
Meeting Agenda

Muscular Dystrophy Coordinating Committee Meeting - 3/18/2024
Time	Presentation
12:00 PM – 12:15 PM	Introductions and Meeting Information Glen Nuckolls, National Institute of Neurological Disorders and Stroke (NINDS/NIH), MDCC DFO
12:15 PM – 12:35 PM	Chair Presentation Robert Carter, Deputy Director, National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS/NIH)
12:35 PM – 12:50 PM	Group Discussion
12:50 PM – 1:05 PM	New member nominee presentation Jennifer Levy – Coalition to Cure Calpain 3 (C3)
1:05 PM – 1:30 PM	Meeting/Conference Reports Muscular Dystrophy Association Clinical and Scientific Conference – March 3-6, 2024 Angela Lek, MDA EveryLife Foundation – Rare Disease Week, Feb 25-March 1, 2024 Annie Kennedy, EveryLife Foundation
1:30 PM – 1:50 PM	Rare Diseases: Considerations for the Development of Drugs and Biological Products Guidance for Industry Cynthia Welch, Office of New Drugs, Center for Drug Evaluation and Research (CDER), U.S. Food & Drug Administration
1:50 PM – 2:00 PM	Break
2:00 PM – 3:50 PM	Exercise in Muscular Dystrophies: Current Understanding and Future Directions “Gaps: Maximizing Health Potential Through Exercise Impact on Neuromuscular Disorders and Clinical Trials” Tanja Taivassalo, Department of Physiology and Functional Genomics, University of Florida (Bio attached) Tina Duong, Division of Neuromuscular Medicine, Stanford University Nicole Voet, Rehabilitation Center Klimmendaal Arnhem, Radboud University Medical Center Nijmegen, the Netherlands “The Molecular Transducers of Physical Activity Consortium (MoTrPAC)” Dan Cooper, Institute for Clinical and Translational Science, Pediatric Exercise and Genomics Research Center, University of California, Irvine
3:50 PM – 4:00 PM	Closing remarks Walter Koroshetz, Director, National Institute of Neurological Disorders and Stroke (NINDS/NIH)
4:00 PM	Adjourn