Skip to main content

MDCC June 19, 2017

meeting_jpg

Upcoming MDCC Meeting

April 30, 2018

Neuroscience Center
Conference Room C/D
6001 Executive Blvd
Bethesda, Maryland 20892

Please note the October 4, 2017 meeting has been canceled.

Monday, June 19, 2017

Neuroscience Center, Conference Room C/D
6001 Executive Blvd.
Bethesda, Maryland 20892

Meeting Agenda

8:30 am

Welcome and introductions

Stephen I. Katz, MDCC Chair and Director
National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS), NIH

8:45 am

Conflict of interest policies and general meeting information

Glen Nuckolls, MDCC Executive Secretary and Program Director
National Institute of Neurological Disorders and Stroke (NINDS), NIH

8:55 am

NICHD and Muscular Dystrophy Research

Diana Bianchi, Director
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD), NIH

Meeting Reports
9:35 am

2017 Muscular Dystrophy Association Scientific Conference

Lianna Orlando, Muscular Dystrophy Association

Meeting on Unique Burdens of Pediatric Clinical Trials

Ryan Fischer, Parent Project Muscular Dystrophy

10:00 am

Break

Topic I: Partnerships in Supporting Training and Career Development

10:15 am

Examples of Partnerships for Training and Career Development in Rheumatic Diseases

Marie Mancini, NIAMS

Brief presentations on support for students, postdocs and clinical fellows:

Tom Cheever, NIAMS
Marielena Mcguire, Congressionally Directed Medical Research Program, Dept. of Defense
Lianna Orlando, Muscular Dystrophy Association
Brian Denger, Parent Project Muscular Dystrophy
Dan Perez, FSH Society
Paul Formaker, Myotonic Dystrophy Foundation

11:45 am

Discussion of opportunities for partnerships supporting research training in the muscular dystrophies

MDCC members and meeting attendees

12:15 pm

Lunch Break

1:00 pm

NIH Initiatives for Early and Mid-Stage Investigators

Stephen I. Katz, Director NIAMS

Topic II: Therapeutic and Assistive Devices for the Muscular Dystrophies

1:15 pm

Session Introduction

Glen Nuckolls, NINDS

Office of Orphan Products Development’s Device Programs for Rare Diseases

Katie Chowdhury, Office or Orphan Products Development, FDA

Regulatory Pathways for Devices

Vasum Peiris, Center for Devices and Radiological Health, FDA

Cardiovascular Devices: Treatment of Duchenne Cardiomyopathy

Linda Cripe, Nationwide Children’s Hospital, Columbus OH

New Technologies in Assistive Devices

Ryan Fischer, Parent Project Muscular Dystrophy

3:30 pm

Discussion of gaps and opportunities for devices for the treatment and management of muscular dystrophies

MDCC members and meeting attendees

4:15 pm

Closing remarks

Stephen I. Katz, MDCC Chair

4:30 pm

Meeting adjourned

Meeting Summary

This Page Last Reviewed on August 22, 2017